Pulse Brain · Growing Health Evidence Index
Tier 3 — Observational / field trialPeer-reviewed

Patient-derived xenografts and organoids model therapy response in prostate cancer

Sofia Karkampouna, Federico La Manna, Andrej Benjak, Mirjam Kiener, Marta De Menna, Eugenio Zoni, Joël Grosjean, Irena Klima, Andrea Garofoli, Marco Bolis, Arianna Vallerga, Jean‐Philippe Theurillat, Maria Rosaria De Filippo, Vera Genitsch, David Keller, Tijmen H. Booij, Christian U. Stirnimann, Kenneth Eng, Andrea Sboner, Charlotte K.Y. Ng, Salvatore Piscuoglio, Peter C. Gray, Martin Spahn, Mark A. Rubin, George N. Thalmann, Marianna Kruithof‐de Julio

Nature Communications · 2021

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Summary

This proof-of-principle study describes the development and characterisation of a novel patient-derived xenograft model (PNPCa) derived from treatment-naïve prostate cancer soft tissue metastasis, harbouring rare BRCA2 and CHD1 somatic mutations with microsatellite instability—a genomic profile present in approximately 3% of advanced prostate cancer cases and previously unmodelled in vivo. Comparative medium-throughput organoid screening of FDA-approved compounds across treatment-naïve and metastatic PDX models revealed differential drug sensitivities, with multikinase inhibitors (ponatinib, sunitinib, sorafenib) demonstrating broad efficacy against organoids from advanced, treatment-resistant cases. The work provides a preclinical tool potentially useful for screening drug responses to both standard-of-care and repurposed compounds in prostate cancer.

UK applicability

This laboratory-based preclinical model development study is not directly applicable to UK farming systems, soil health, or food production. Its relevance to Vitagri's Pulse Brain catalogue on agricultural systems and nutrition is not evident from the content.

Key measures

Transcriptomic and genomic profiling (RNA sequencing, whole-exome sequencing); drug sensitivity screening of FDA-approved compounds; identification of multikinase inhibitor efficacy

Outcomes reported

The study developed and characterised patient-derived xenograft (PDX) and organoid models of prostate cancer harbouring BRCA2, CHD1 mutations and microsatellite instability, and screened FDA-approved compounds to identify differential drug sensitivities across treatment-naïve and metastatic PDX models.

Theme
General food systems / other
Subject
Other / interdisciplinary
Study type
Research
Study design
Laboratory experimental study with medium-throughput organoid drug screening
Source type
Peer-reviewed study
Status
Published
System type
Laboratory / in vitro
DOI
10.1038/s41467-021-21300-6
Catalogue ID
SNmoh0dslh-c3pjfs

Topic tags

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