Pulse Brain · Growing Health Evidence Index
Tier 3 — Observational / field trialPeer-reviewed

Pembrolizumab monotherapy for high-risk non-muscle-invasive bladder cancer without carcinoma in situ and unresponsive to BCG (KEYNOTE-057): a single-arm, multicentre, phase 2 trial

Andrea Necchi, M. Roumiguié, Ashish M. Kamat, Neal D. Shore, Joost L. Boormans, Adil Esen, Thierry Lebrét, Shuya Kandori, Dean F. Bajorin, Laurence E. Krieger, Scot A. Niglio, Edward Uchio, Ho Kyung Seo, Ronald de Wit, Eric A. Singer, Petros Grivas, Hiroyuki Nishiyama, Haojie Li, Pranshu Baranwal, Margot Van den Sigtenhorst-Fijlstra, Ekta Kapadia, Girish S. Kulkarni

The Lancet Oncology · 2024

Read source ↗ All evidence

Summary

KEYNOTE-057 was a phase 2 trial investigating pembrolizumab monotherapy as a treatment option for patients with high-risk non-muscle-invasive bladder cancer lacking carcinoma in situ and refractory to BCG immunotherapy. As suggested by the trial design and journal, the study provides efficacy and safety data to support clinical decision-making in this difficult-to-treat patient population. The findings may inform treatment sequencing and immunotherapy approaches in BCG-unresponsive bladder cancer.

UK applicability

The findings are relevant to UK urological oncology practice, as BCG-unresponsive bladder cancer represents a significant clinical challenge in the National Health Service. Pembrolizumab approval and reimbursement for this indication would depend on Health Technology Assessment review, cost-effectiveness analysis relative to other options (such as radical cystectomy), and alignment with National Institute for Health and Care Excellence guidance.

Key measures

Complete response rate, recurrence-free survival, disease-free survival, adverse events, tolerability

Outcomes reported

The study evaluated the efficacy and safety of pembrolizumab monotherapy in patients with high-risk non-muscle-invasive bladder cancer who had failed BCG treatment. Primary outcomes likely included complete response rates, recurrence-free survival, and adverse event profiles.

Theme
General food systems / other
Subject
Other / interdisciplinary
Study type
Research
Study design
Phase 2 single-arm multicentre trial
Source type
Peer-reviewed study
Status
Published
Geography
International
System type
Human clinical
DOI
10.1016/s1470-2045(24)00178-5
Catalogue ID
SNmoh0dubp-1bnqx2

Topic tags

Pulse AI · ask about this record

Dig deeper with Pulse AI.

Pulse AI has read the whole catalogue. Ask about this record, its theme, or how the findings apply to UK farming and policy — every answer cites the underlying studies.